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Acknowledgements
The authors report the shared opinion of the scientists and clinicians who developed and performed gene therapy of SCIDs in France, Italy and the United Kingdom, and in particular of Alessandro Aiuti, Claudio Bordignon, Alain Fischer, Salima Hacein-Bey-Abina and Maria Grazia Roncarolo.
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Cavazzana-Calvo, M., Thrasher, A. & Mavilio, F. The future of gene therapy. Nature 427, 779–781 (2004). https://doi.org/10.1038/427779a
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DOI: https://doi.org/10.1038/427779a
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