Table. 1 Subject-, disease- and transplant-related variables.

From: Therapy of posttransplant poor graft function with eltrombopag

Number

Age

Sex

Underlying disease

Conditioning

GvHD prevention

Graft source

CD34 × 10E + 6/kg

D–R ABO mismatch

Prior therapy

Dose/w (mg)

Best response

Disease state

Survivals

1

60

M

MDS

Flu /TBI

CSA/MMF

PBSC

4.4

No

SDP, IGIV, G-CSF

350

NoR

CR

Dead

2

34

M

AA

CY/ATG

CSA/MTX

PBSC

2.75

No

SDP, IGIV, G-CSF

350

CR

CR

Alive

3

47

M

MDS

Bu/CY/ATG

TAC/MMF

PBSC

6

No

SDP, IGIV, G-CSF

700

NoR

CR

Alive

4

48

F

AML

Flu/CY/TBI

CSA/MMF/PTCY

PBSC

4.2

No

SDP,IVIG, G-CSF

700

NoR

CR

Dead

5

43

F

HL

Flu/Bu

CSA/MMF

PBSC

4.76

Yes

SDP, IGIV

525

CR

CR

Dead

6

8

M

AA

Flu/CY/TBI/ATG/PTCY

TAC/MMF/PTCY

BM

9.19

Yes

SDP, IGIV,G-CSF

700

NoR

CR

Alive

7

47

F

AML

Flu/CY/TBI/PTCY

CSA/MMF

PBSC

6.56

No

SDP, G-CSF

350

NoR

CR

Dead

8

49

F

ALL

BuCY/TBI/PTCY

TAC/MMF/PTCY

BM

4.32

Yes

SDP

700

CR

CR

Alive

9

28

M

HL

Flu/CY/TBI

CSA/MMF

PBSC

6.2

No

SDP

350

CR

NCR

Dead

10

45

F

AML

Bu/CY

CSA/MTX

PBSC

6.45

Yes

SDP, IGIV, G-CSF

450

CR

CR

Alive

11

61

F

PMF

TBF

TAC/MTX

PBSC

8.88

Yes

SDP, IGIV, G-CSF

525

CR

CR

Alive

12

26

M

DC

Flu/CY/TBI/ATG

TAC/MMF

BM

4.58

Yes

SDP, IGIV

350

CR

CR

Alive

13

26

F

FA/MDS

Flu/CY/TBI/ATG

TAC/MMF

BM

2.63

No

SDP, IGIV

625

CR

CR

Alive

14

37

M

HL

Flu/CY/TBI/PTCY

CSA/MMF/PTCY

PBSC

9.48

No

IGIV

700

NoR

CR

Alive

  1. PGF poor graft function, MDS myelodysplastic syndrome, AA aplastic anaemia, AML acute myeloid leukemia, HL Hodgkin lymphoma, ALL acute lymphoblastic leukemia, PMF primary myelofibrosis, FA Fanconi anaemia, DC Deskeratosis congenita, Flu fludarabine, TB total body irradiation, CY cyclophosphamide, ATG anti-thymocyte globulin, BU busulfan, PTCY posttransplant cyclophosphamide, T thiotepa, CSA cyclosporine, MM mycophenolate mofetil, BCT blood cells transplant, BM bone marrow, BMT bone marrow transplant, D–R ABO mismatch donor–recipient ABO mismatch, SDP single-donor platelet, IVIG intravenous immunoglobulin, G-CSF granulocyte colony-stimulating factor, CR complete response, NR no response.