Table 6 Non-relapse mortality cumulative incidence, relapse incidence, progression-free survival (GvHD-free relapse-free survival and overall survival.
Variables | Modalities | n | 6y NRM | 6y RI | 6y PFS | 6y GRFS | 6y OS |
---|---|---|---|---|---|---|---|
Total | [2000–2022] | 35 | 18 [7.1–32.8] | 15.9 [5.6–30.9] | 66.1 [47–79.7] | 50 [30.6–66.7] | 71.1 [51.4–84] |
Year of HCT | [2000–2007] | 16 (45.7) | 25 [7.2–48.1] | 25 [7.2–48.2] | 50 [24.5–71] | 41.7 [17.4–64.5] | 56.2 [29.5–76.2] |
[2008–2022] | 19 (54.3) | 10.5 [1.7–29] | 5.3 [0.3–22.1] | 84.2 [58.7–94.6] | 62.3 [34–81.3] | 89.5 [64.1–97.3] | |
P value | 0.37 | 0.18 | 0.09 | 0.58 | 0.09 | ||
Age at HCT | (0–6) | 19 (54.3) | 12.8 [1.8–34.8] | 12.1 [1.8–33.2] | 75.1 [45.6–90.1] | 63 [30.9–83.4] | 79.5 [48.1–93.1] |
[7–18) | 16 (45.7) | 25 [7.3–48] | 18.8 [4.2–41.3] | 56.2 [29.5–76.2] | 37.5 [15.4–59.8] | 61.1 [32.7–80.5] | |
P value | 0.3 | 0.66 | 0.21 | 0.053 | 0.22 | ||
Recipient sex | Male | 23 (65.7) | 25 [7.2–48.1] | 20.6 [5.9–41.4] | 55.6 [31.1–74.4] | 40.9 [18.5–62.3] | 63.9 [37.9–81.3] |
Female | 12 (34.3) | 10.5 [1.7–29] | 8.3 [0.4–32.4] | 83.3 [48.2–95.6] | 66.7 [33.7–86] | 83.3 [48.2–95.6] | |
P value | 0.37 | 0.35 | 0.12 | 0.24 | 0.28 | ||
Months between diagnosis and HCT | [1–8) | 19 (54.3) | 16.8 [3.9–37.6] | 17.5 [4–38.9] | 65.7 [38.8–83] | 52.7 [26.7–73.3] | 71.3 [44.1–87] |
[9–136] | 16 (45.7) | 18.8 [4.3–41.1] | 13.8 [2–36.7] | 67.5 [38.4–85.1] | 48.2 [20.8–71.2] | 72.7 [42–88.9] | |
P value | 0.78 | 0.84 | 0.87 | 0.49 | 0.86 | ||
Donor type | MSD | 17 (48.6) | 12.6 [1.9–34.1] | 13 [1.9–34.9] | 74.3 [45–89.6] | 67 [37.9–84.7] | 73.7 [43.9–89.3] |
Other | 18 (51.4) | 22.2 [6.6–43.6] | 18.9 [4.1–41.9] | 58.8 [32–78.1] | 34.9 [12.4–58.8] | 69.3 [40.6–86.2] | |
P value | 0.42 | 0.56 | 0.24 | 0.07 | 0.6 | ||
Source of HCs | BM | 15 (42.9) | 0% | 14.9 [2.2–38.9] | 85.1 [52.3–96.1] | 70.1 [38.5–87.6] | 90.9 [50.8–98.7] |
Other | 20 (57.1) | 32 [12.3–53.9] | 17.1 [3.8–38.5] | 50.8 [26.3–71] | 36.1 [14.5–58.4] | 54 [28.1–74.2] | |
P value | 0.02 | 0.81 | 0.03 | 0.09 | 0.01 |