Extended Data Table 2 Summary of non-ocular AEs

From: Intravitreal antisense oligonucleotide sepofarsen in Leber congenital amaurosis type 10: a phase 1b/2 trial

  1. *Adults n = 3, children n = 3. †Adults n = 3, children n = 2. ‡Adults n = 6, children n = 5. §Pain comprised whole body pain for one patient; mild body pain and paranasal sinus discomfort were reported in a second patient. ¶An accident with a belt sander was reported. ‖Severe laceration of the fifth finger of the right hand was reported and linked to the accident and not related to the study drug. **A double dose of anti-epileptic drug was administered.
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