Table 1 Edits of the FGF20 gene based on ssODN donor used for allelic repair in single-cell clones targeted with Sca-ssODN and SpCas9 or SpCas9-HF1 (Supplementary FigsĀ S4 and S5).
Clone genotype | Sca/Sca | Sca/Sca*Wt | Sca/INDEL | INDEL/INDEL | Total |
|---|---|---|---|---|---|
SpCas9-WT clones | 0 | 0 | 3 (7.9%) | 35 (92.1%) | 38 (100%) |
SpCas9-HF1 clones | 14 (36.8%) | 2 (5.3%) | 7 (18.4%) | 15 (39.5%) | 38 (100%) |
HDR | Biallelic | Biallelic | Monoallelic | N/A | N/A |