Table 1 Patient characteristics.

From: Eltrombopag for the treatment of refractory thrombocytopenia associated with connective tissue disease

Patient

Age, years

Sex

Protopathy

Diagnosis time for protopathy

Diagnosis time for thrombocytopenia

Lowest platelet counts(× 109/L)

Previous treatments

Complications

Acompanying diseases

APS

Reticulocytes ratio (%)

Bone marrow puncture

SLEDAI

1

54

F

SLE

1988

2014

2

Pred,CysA, CTX, IVIG, vincristine, transfused platelets

No

Hypertension Diabetes

Yes

2.14

NA

3

2

54

F

SLE

2005

2005

12

Pred, CysA

No

HBC,Spleno-megaly, Hyperthyroid-ism

No

NA

NA

 

3

31

F

SLE

2005

2005

5

Pred, CysA, AZA

No

No

No

NA

NA

 

4

47

F

UCTD

2015

2015

9

Pred, CysA

No

No

No

3.97

NA

1

5

42

F

SS

2016

2016

7

Pred, HCQ, CysA, IVIG, TPO

No

No

No

2.74

AA

 

6

37

F

SLE

2013

2018

1

Pred, HCQ, CysA, MMF, IVIG, splenectomy

Autoimmune hemolytic anemia

No

No

2.31

Normal

1

7

22

F

SLE

2018

2018

9

Pred, CysA, TPO

No

No

No

1.23

ITP

5

8

16

M

SLE

2017

2017

3

Pred, CysA, IVIG

No

No

No

2.47

ITP

3

9

40

F

SLE

2018

2018

1

Pred, HCQ, CysA, IVIG, RTX

PAH

No

No

5.24

ITP

5

10

53

F

SS

2003

2003

4

Pred, HCQ, transfused platelets

No

No

No

3.39

Megakaryocytopen-ia

 

11

63

M

UCTD

2019

2019

3

Pred, CysA, IVIG, TPO

No

No

No

1.73

Normal

 

12

54

F

SS

2018

2018

2

Pred, CysA, IVIG, TPO

No

Ovarian cancer

No

0.55

Megakar-yocyte deficiency

 

13

27

F

SLE

2014

2014

10

Pred, CysA, IVIG, CTX, RTX, plasma exchange

No

No

No

1.76

MAS

16

14

22

M

UCTD

2015

2015

10

Pred

No

No

No

NA

ITP

 

15

47

F

SLE

2018

2018

12

Pred, CysA

No

No

No

NA

ITP

1

  1. F female, M male, SLE systemic lupus erythematosus, SS sjogren's syndrome, UCTD undifferentiated connective tissue disease, Pred prednisolone, CysA cyclosporin A, AZA azathioprine, HCQ hydroxychloroquine, IVIG intravenous immunoglobulin, MMF mycophenolate mofetil, TPO thrombopoietin, RTX rituximab, CTX cyclophosphamide, PAH pulmonary hypertension, APS anticardiolipin antibody syndrome, ITP idiopathic thrombocytopenia, MAS hemophagocytic syndrome, HBC hepatitis B cirrhosis, SLEDAI systemic lupus erythematosus disease activity index, NA non acceptance.