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Advanced filters: Author: Fabrice Monpoux Clear advanced filters

  • The final report of the phase 1/2 lentiviral gene therapy trial in severe β-hemoglobinopathies, HGB-205, shows a long-term safety profile and sustained reduction of transfusion requirements in patients with β-thalassemia and of sickle cell crises in patients with sickle cell disease.

    • Elisa Magrin
    • Michaela Semeraro
    • Marina Cavazzana
    Research
    Nature Medicine
    Volume: 28, P: 81-88