Extended Data Table 2 Number of skills gained, improved and maintained at week 52 as measured by the NSAA (modified intent-to-treat population)

From: AAV gene therapy for Duchenne muscular dystrophy: the EMBARK phase 3 randomized trial

  1. Skills are gained when the average item score is 0 at baseline and >0 at Part 1 week 52; skills are improved when the average item score at baseline is >0 but less than the average item score at Part 1 week 52; and skills are maintained when the average item scores at baseline and Part 1 week 52 are the same and >0.
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