Extended Data Table 2 Statistical analysis using linear mixed model showing fixed effects of treatment and treatment over time for brain, ventricle volumes in the treated GM2 infantile patients compared to untreated patients

From: Dual-vector rAAVrh8 gene therapy for GM2 gangliosidosis: a phase 1/2 trial

  1. The F-statistic and p values are reported along with the magnitude effect in volumetric change (NS – not significant).