Table 1 Baseline patient characteristics.
Patients (N = 40) | |
|---|---|
Age | |
Median (IQR) age at initial diagnosis, years [mean ± SD] | 3.5 (2.4–5.4) [3.9 ± 2.3] |
Median (IQR) age at informed consent, years [mean ± SD] | 6.0 (4–7.5) [6.4 ± 3.5] |
Sex | |
Male | 28 (70) |
Female | 12 (30) |
Race, white | 40 (100) |
Disease status | |
Relapsed | 23 (57) |
Refractory | 17 (43) |
Relapses since initial diagnosis | |
None | 17 (43) |
1 | 19 (48) |
2 | 4 (10) |
INSS stage at initial diagnosis | |
1 | 2 (5) |
2 | 0 |
3 | 2 (5) |
4 | 36 (90) |
MYCN amplification | |
No | 32 (80) |
Yes | 7 (18) |
Missing | 1 (3) |
Bone marrow involvement | 14 (35) |
Soft tissue involvement | 17 (43) |