Fig. 2: Correction of NPC DM1 phenotypes after a treatment with the IONIS 486178 ASO.

A FISH immunofluorescence showing the destruction of nuclear foci and the redistribution of MBNL1 and B MBNL2 24 h after transfection with 500 nM IONIS 486178 ASO. C RT-PCR of DM1 alternative mis-splicing. Statistical analyses were performed using an ordinary one-way ANOVA with Tukey’s multiple comparisons test. The error bars are presented as the mean ± SEM. Scale bar: 20 µm.