Fig. 3: Competitive transduction assay to compare efficiency of barcoded rAAV promoters in rats.

SD rats (6–8 week male) were injected with a rAAV promoter kit packaged in AAV6 (n = 5) and AAV9 (n = 4) at 5 × 1011 vg via the tail vein. Four weeks post transduction, rats were sacrificed. A Heart and B liver tissues were collected for DNA/RNA extraction followed by NGS analysis. For each capsid and tissue combination, results on the left are displayed as boxplots comparing performance of ubiquitous promoter CMV, liver-specific promoter (LSP) and cardiac-specific promoters (CSP), and on the right as boxplots comparing performance of cardiac-specific promoters only. Statistical analyses were performed using the Kruskal-Wallis test followed by Dunn’s post-hoc test with Bonferroni correction (*p < 0.05).