Fig. 2: Progression of gross motor function measure (GMFM) in each patient with increasing dose.

20 eow: 20 mg/kg every other week, 40 eow: 40 mg/kg every other week; 30 w: 30 mg/kg weekly; 40 w: 40 mg/kg weekly.

20 eow: 20 mg/kg every other week, 40 eow: 40 mg/kg every other week; 30 w: 30 mg/kg weekly; 40 w: 40 mg/kg weekly.