Table 1 Patient demographics and tumor characteristics grouped by originating institution.

From: Sequential genomic analysis using a multisample/multiplatform approach to better define rhabdomyosarcoma progression and relapse

Variable

Curie, N = 15

MSK, N = 20

Total, N = 35

Age groupa

 Pediatric

10 (66.7%)

9 (45.0%)

19 (54.3%)

 Adolescent/Young adult

5 (33.3%)

11 (55.0%)

16 (45.7%)

Sex

 Female

9 (60.0%)

9 (45.0%)

18 (51.4%)

 Male

6 (40.0%)

11 (55.0%)

17 (48.6%)

Site

 Head and neck

5 (33.3%)

8 (40.0%)

13 (37.1%)

 Abdominopelvis

3 (20.0%)

4 (20.0%)

7 (20.0%)

 Extremity

7 (46.7%)

6 (30.0%)

13 (37.1%)

 Thorax

0 (0.0%)

2 (10.0%)

2 (5.7%)

Histology/Fusion

 Fusion-Positive RMS

8 (53.3%)

10 (50.0%)

18 (51.4%)

 Fusion-Negative RMS

7 (46.7%)

10 (50.0%)

17 (48.6%)

Size

 ≤5 cm

7 (47.0%)

4 (20.0%)

11 (31%)

 >5 cm

8 (53.0%)

16 (80.0%)

24 (69%)

N (TNM Classification)

 0

5 (33%)

11 (55%)

16 (46%)

 1

10 (77%)

9 (45%)

19 (54%)

 M (TNM Classification)

 0

9 (60%)

15 (75.0%)

24 (69%)

 1

6 (40%)

5 (25.0%)

11 (31%)

RMS Risk group (COG)

 High

13 (87%)

12 (60.0%)

25 (71%)

 Intermediate

2 (13%)

7 (35.0%)

9 (26%)

 Low

0 (0.0%)

1 (5.0%)

1 (3%)

Relapse site

 Local

6 (42.9%)

9 (47.4%)

15 (45.5%)

 Metastatic

8 (57.1%)

7 (36.8%)

15 (45.5%)

 Regional

0 (0.0%)

3 (15.8%)

3 (9.1%)

 NA

1

1

2

5-year Overall Survival rates [95% IC]

31% [13–73]

35% [13–89]

33% [18–62]

  1. aPediatric: 0–11 years; adolescent/young adult >12 years.