Fig. 3: Total plasma and urine globotriaosylceramide (Gb3) and lyso-Gb3 levels.

Plasma Gb3 (a), plasma lyso-Gb3 (b), urine Gb3 (c), and urine lyso-Gb3 (d) levels are illustrated for each patient. Red arrow is at Day −30 when ET was stopped prior to mobilization. Green arrow is at Day 30 when ET was restarted for Patients 1, 2, 4, and 5. The orange arrow demarks when Patient 4 stopped ET at Day 214 and the blue arrow is when Patient 1 stopped ET at Day 548. Patient 3 chose not to restart ET.