Table 3 Developmental milestones after gene delivery.

From: Gene therapy for aromatic L-amino acid decarboxylase deficiency by MR-guided direct delivery of AAV2-AADC to midbrain dopaminergic neurons

Subject

Follow-up duration (months)

Head control

Sit independently

Reach and grasp

Walk with 2-hand support

Baseline

Post-surgery

(month attained)

Baseline

Post-surgery

(month attained)

Baseline

Post-surgery

(month attained)

Baseline

Post-surgery

(month attained)

1

36

No

No

No

No

No

No

No

No

2

33

±

Yes (2)

No

Yes (7)

No

Yes (10)

No

Yes (17)

3

30

No

Yes (12)

No

Yes (21)

No

No

No

No

4

22

No

Yes (7)

No

Yes (11)

No

Yes (10)

No

No

5

20

±

Yes (3)

No

Yes (7)

Yes

Yes

No

Yes (18)

6

7

No

Yes (2.5)

No

Yes (7)

No

No

No

No

7

7

No

Yes (4)

No

No

No