The recent failure of a gene therapy for Huntington’s disease was devastating for patients, but researchers remain optimistic.
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Arnold, C. Record number of gene-therapy trials, despite setbacks. Nat Med 27, 1312–1315 (2021). https://doi.org/10.1038/s41591-021-01467-7
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DOI: https://doi.org/10.1038/s41591-021-01467-7