Abstract
MET exon 14 skipping mutations (METex14) or amplification drives a subset of non-small cell lung cancer (NSCLC). Tepotinib, a selective MET tyrosine kinase inhibitor (TKI), has shown promise in early trials; however, comparative efficacy and safety data across MET-altered subpopulations remain limited. This systematic review of six studies (546 patients) assessed the clinical outcomes of Tepotinib in METex14 or MET-amplified NSCLC. The primary endpoint was objective response rate (ORR); secondary endpoints included disease control rate (DCR), progression-free survival (PFS), overall survival (OS), and safety. The pooled objective response rate (ORR) was 52% (95% CI: 48–56%) and a disease control rate (DCR) of 76% (95% CI: 72–80%). Median PFS was 10.16 months, and median OS was 14.67 months. Subgroup analyses revealed no significant differences in ORR between METex14 (52%) and MET amplification (53%, p = 0.905) or between monotherapy (51%) and combination therapy (56%, p = 0.242). Common treatment-related adverse events (TRAEs) were grade 1–2 peripheral edema (50%) and diarrhea (36%); grade ≥ 3 TRAEs were infrequent (8% for edema). In conclusion, Tepotinib demonstrated comparable efficacy in METex14 and MET-amplified NSCLC with a manageable safety profile. The PFS benefit of combination therapy warrants further randomized trials. These findings support Tepotinib as a valuable therapeutic option for MET-altered NSCLC.
Data availability
All data supporting the findings are included in the manuscript and supplementary files. Extracted data for the meta-analysis are available from the corresponding author upon reasonable request.
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Funding
The work was supported by the Natural Science Foundation of Gansu Province [grant number 25JRRA588]; the Gansu Health Industry Scientific Research Program [grant number GSWSKY2021-061]; and Lanzhou University Second Hospital’s Cuiying Scientific Training Program for Undergraduates [grant numbers CYXZ2022-35 and CYXZ2023-23].
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Conception and design: JYX and QYC. Acquisition of data: JYX and XYL. Critical revision of the manuscript for important intellectual content: JYX, DGZ, and QYC. Statistical analysis: JYX and QYC. Obtain funding: DGZ. All authors contributed to the article and approved the submitted version.
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Xiao, J., Cai, Q., Li, X. et al. Efficacy and safety of tepotinib in MET‑altered non‑small cell lung cancer: a meta-analysis. Sci Rep (2026). https://doi.org/10.1038/s41598-026-41989-z
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DOI: https://doi.org/10.1038/s41598-026-41989-z