Extended Data Fig. 7: Part B infantile-onset cohort – CHOP-INTEND sensitivity analyses.
From: High-dose nusinersen for spinal muscular atrophy: a phase 3 randomized trial

CHOP-INTEND, Children’s Hospital of Philadelphia Infant Test of Neuromuscular Disorders; CI, confidence interval; ITT, intent-to-treat; LS, least-squares; MI, multiple imputation; PP, per protocol.