AAV9-DARS2 Gene Therapy Rescues Phenotype in Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation Patient Cells and Neuronal Dars2 Deficient Mice

Journal:
Annals of Neurology
Published:
DOI:
10.1002/ana.78037
Affiliations:
3
Authors:
8
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Institutions Authors Share
Kennedy Krieger Institute, United States of America (USA)
4.000000
 0.50
University of Maryland, Baltimore (UMB), United States of America (USA)
3.000000
 0.38
Johns Hopkins University (JHU), United States of America (USA)
1.000000
 0.13
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