Liver-directed lentiviral gene therapy confers durable hepatic and systemic amelioration of methylmalonic acidemia in mice

Journal:

Journal of Hepatology

Published:

2026-05-25

DOI:

10.1016/j.jhep.2026.05.011

Affiliations:

9

Authors:

19

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Institutions	Authors	Share
San Raffaele Telethon Institute for Gene Therapy (HSR-TIGET), Italy	9.000000	0.47
University of Colorado Anschutz Medical Campus (CU Anschutz), United States of America (USA)	3.000000	0.16
San Raffaele Scientific Institute, Italy	2.500000	0.13
Vita-Salute San Raffaele University (UniSR), Italy	2.000000	0.11
IRCCS Meyer Children's Hospital, Italy	1.000000	0.05
Genespire, Italy	1.000000	0.05
University of Florence (UNIFI), Italy	0.500000	0.03

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