Gmppb-mutant mice exhibit dystroglycanopathy symptoms that are rescued with GSK3β inhibition or AAV-mediated GMPPB gene replacement

Journal:
Nature Communications
Published:
Affiliations:
10
Authors:
18
Institutions Authors Share
Fudan University, China
8.000000
0.44
The Fifth People's Hospital of Shanghai, Fudan University, China
2.000000
0.11
MOE Key Laboratory of Marine Drugs, OUC, China
2.000000
0.11
MOE Key Laboratory of Metabolism and Molecular Medicine, Fudan University, China
1.500000
0.08
National Medical Products Administration (NMPA), China
1.000000
0.06
Huashan Hospital, Fudan University, China
1.000000
0.06
Keymed Biosciences, China
1.000000
0.06
Shanghai Pudong Hospital, Fudan University, China
1.000000
0.06
State Key Laboratory of Genetic Engineering, Fudan University, China
0.500000
0.03