Long-term comparative analysis of AAV9-mediated gene replacement therapies for spinal muscular atrophy in mice

Journal:
Nature Communications
Published:
Affiliations:
6
Authors:
28
Institutions Authors Share
University of Massachusetts Chan Medical School (UMass Chan Medical School), United States of America (USA)
26.000000
26.000000
26.000000
0.93
CANbridge Pharmaceuticals, United States of America (USA)
2.000000
0.07