Safety and efficacy analysis of in vivo lentiviral gene therapy in pre-clinical ARC syndrome models

Journal:

Nature Communications

Published:

2026-06-19

DOI:

10.1038/s41467-026-73631-x

Affiliations:

7

Authors:

22

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Institutions	Authors	Share
UCL, United Kingdom (UK)	12.666667 12.666667	0.58
NIHR Great Ormond Street Hospital BRC, United Kingdom (UK)	5.166667	0.23
UCL EGA Institute for Women's Health (IfWH), United Kingdom (UK)	2.000000	0.09
UCL/MRC Laboratory for Molecular Cell Biology (LMCB), United Kingdom (UK)	1.000000	0.05
Great Ormond Street Hospital for Children NHS Trust, United Kingdom (UK)	0.666667	0.03
Royal Free Hospital, United Kingdom (UK)	0.500000	0.02