The UBE3A-ATS antisense oligonucleotide rugonersen in children with Angelman syndrome: a phase 1 trial

Journal:
Nature Medicine
Published:
Affiliations:
26
Authors:
48
Institutions Authors Share
F. Hoffmann-La Roche Ltd., Switzerland
28.000000
28.000000
28.000000
0.58
Roche Products Limited, United Kingdom (UK)
4.000000
0.08
The University of North Carolina at Chapel Hill (UNC), United States of America (USA)
2.000000
0.04
Texas Children's Hospital, BCM, United States of America (USA)
1.000000
0.02
Erasmus University Medical Center (Erasmus MC), Netherlands
1.000000
0.02
New University of Lisbon (UNL), Portugal
1.000000
0.02
Sant Joan de Déu Research Institute (IRSJD), Spain
1.000000
0.02
Rush University Medical Center, United States of America (USA)
1.000000
0.02
Mayo Clinic, United States of America (USA)
1.000000
0.02
Virgen del Rocío University Hospital, Spain
1.000000
0.02
IRCCS Bambino Gesù Children's Hospital, Italy
1.000000
0.02
UCLA Mattel Children's Hospital, United States of America (USA)
1.000000
0.02
USC Children's Hospital Los Angeles (CHLA), United States of America (USA)
1.000000
0.02
IRCCS San Raffaele Hospital (HSR), Italy
1.000000
0.02
Rady Children's Hospital-San Diego, United States of America (USA)
0.500000
0.01
University of California, San Diego (UC San Diego), United States of America (USA)
0.500000
0.01
Research Centers of Catalonia (CERCA), Spain
0.500000
0.01
Institut d’Investigació i Innovació Parc Taulí (I3PT), Spain
0.500000
0.01
Columbia University Irving Medical Center (CUIMC), CU, United States of America (USA)
0.500000
0.01
New York-Presbyterian Morgan Stanley Children's Hospital, United States of America (USA)
0.500000
0.01