In vivo base editing gene therapy for heterozygous familial hypercholesterolemia: a phase 1 trial

Journal:
Nature Medicine
Published:
Affiliations:
8
Authors:
16
Institutions Authors Share
YolTech, China
6.000000
0.38
Renji Hospital, SJTU, China
5.750000
0.36
East China Normal University (ECNU), China
1.500000
0.09
Ruijin Hospital, SJTU, China
1.250000
0.08
Hannover Medical School (MHH), Germany
1.000000
0.06
Shanghai Jiao Tong University (SJTU), China
0.500000
0.03