AAV9-Mediated Gene Therapy for Infantile-Onset Pompe’s Disease

Journal:

The New England Journal of Medicine

Published:

2025-06-26

DOI:

10.1056/nejmoa2407766

Affiliations:

9

Authors:

28

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Institutions	Authors	Share
The Seventh Medical Center, PLAGH, China	13.000000 13.000000	0.46
Genecradle Therapeutics, China	8.000000	0.29
The People's Liberation Army General Hospital (PLAGH), China	5.000000	0.18
Children's Hospital, Zhejiang University School of Medicine, China	1.000000	0.04
Beijing Children's Hospital, Capital Medical University, China	1.000000	0.04

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