Single Antisense Oligonucleotides Correct Diverse Splicing Mutations in Hotspot Exons

Journal:
Proceedings of the National Academy of Sciences of the United States of America
Published:
Affiliations:
8
Authors:
9
Institutions Authors Share
Brown University, United States of America (USA)
6.000000
0.67
Autism and Developmental Medicine Institute (ADMI), GHS, United States of America (USA)
1.000000
0.11
Geisinger Health System (GHS), United States of America (USA)
1.000000
0.11
MRC Laboratory of Medical Sciences (LMS), United Kingdom (UK)
0.500000
0.06
Imperial College London (ICL), United Kingdom (UK)
0.500000
0.06