BMN 349, a small molecule inhibitor of Z alpha-1 antitrypsin polymerization, increases secretion and reduces intrahepatic inclusions in a mouse model of disease.

Journal:
Hepatology
Published:
Affiliations:
4
Authors:
22
Institutions Authors Share
BioMarin Pharmaceutical, Inc., United States of America (USA)
18.000000
18.000000
0.82
UCL, United Kingdom (UK)
3.000000
0.14
Queen's University, Canada
1.000000
0.05