Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2

Journal:: Science Advances
Published:: 2025-11-14
DOI:: 10.1126/sciadv.ady6760
Affiliations:: 4
Authors:: 10

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Institutions	Authors	Share
Duke University Health System, United States of America (USA)	10.000000 10.000000	1.00

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