Self-inactivating AAV-CRISPR at different ages enables sustained amelioration of Huntington’s disease deficits in BAC226Q mice

Journal:
Science Advances
Published:
DOI:
10.1126/sciadv.aea8052
Affiliations:
1
Authors:
9
Institutions Authors Share
MOE Key Laboratory of Cell Proliferation and Differentiation, PKU, China
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