Self-inactivating AAV-CRISPR at different ages enables sustained amelioration of Huntington’s disease deficits in BAC226Q mice
- Journal:
- Science Advances
- Published:
- DOI:
- 10.1126/sciadv.aea8052
- Affiliations:
- 1
- Authors:
- 9
| Institutions | Authors | Share |
|---|---|---|
| MOE Key Laboratory of Cell Proliferation and Differentiation, PKU, China | 1.00 |