Patient-derived models of UBA5-associated encephalopathy identify defects in neurodevelopment and highlight potential therapeutic avenues

Journal:: Science Translational Medicine
Published:: 2025-05-07
DOI:: 10.1126/scitranslmed.adn8417
Affiliations:: 4
Authors:: 13

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Institutions	Authors	Share
St. Jude Children's Research Hospital (St. Jude), United States of America (USA)	13.000000 13.000000	1.00

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