Functional correction of the untreatable CFTR 1717-1G>A mutation through mRNA- and sgRNA-optimized base editing

Journal:
Science Translational Medicine
Published:
DOI:
10.1126/scitranslmed.adw8886
Affiliations:
6
Authors:
14
Go to article
Institutions Authors Share
University of Trento (UNITN), Italy
7.000000
 0.50
Catholic University of Leuven (KU Leuven), Belgium
4.000000
 0.29
Telethon Institute of Genetics and Medicine (TIGEM), Italy
2.000000
 0.14
Institute of Biophysics (IBF), CNR, Italy
1.000000
 0.07
Interested in Cardiovascular Medicine and Haematology?