Restoration of progranulin by engineered hematopoietic stem cell–derived microglia corrects phenotypes of granulin knockout mice

Journal:
Science Translational Medicine
Published:
Affiliations:
4
Authors:
11
Institutions Authors Share
University of Padova (UNIPD), Italy
4.500000
0.41
Fondazione Istituto di Ricerca Pediatrica Città della Speranza (IRP), Italy
4.500000
0.41
Orchard Therapeutics, United Kingdom (UK)
1.000000
0.09
Altheia Science, Italy
1.000000
0.09