Preclinical evaluation of antisense oligonucleotide therapy in a mouse model of HNRNPH2-related neurodevelopmental disorder

Journal:
Science Translational Medicine
Published:
Affiliations:
5
Authors:
13
Institutions Authors Share
St. Jude Children's Research Hospital (St. Jude), United States of America (USA)
10.000000
10.000000
0.77
Ionis Pharmaceuticals, United States of America (USA)
3.000000
0.23