RNA-LNP–mediated in vivo prime editing corrects disease phenotypes in a mouse model of citrullinemia type I

Journal:
Science Translational Medicine
Published:
Affiliations:
6
Authors:
23
Institutions Authors Share
University of Zurich (UZH), Switzerland
11.000000
11.000000
0.48
University Children's Hospital of Zurich, Switzerland
4.000000
0.17
Acuitas Therapeutics, Canada
3.000000
0.13
University of Pennsylvania (Penn), United States of America (USA)
3.000000
0.13
Swiss Federal Institute of Technology Zurich (ETH Zurich), Switzerland
2.000000
0.09