Cross-species efficacy of AAV-mediated ARSA replacement for Metachromatic Leukodystrophy
- Journal:
- Journal of Clinical Investigation
- Published:
- DOI:
- 10.1172/jci185001
- Affiliations:
- 3
- Authors:
- 29
| Institutions | Authors | Share |
|---|---|---|
| Bioverativ, Inc., United States of America (USA) | 0.69 | |
| Sanofi Pasteur, United States of America (USA) | 0.24 | |
| Sanofi US, United States of America (USA) | 0.07 |