Cross-species efficacy of AAV-mediated ARSA replacement for Metachromatic Leukodystrophy

Journal:
Journal of Clinical Investigation
Published:
Affiliations:
3
Authors:
29
Institutions Authors Share
Bioverativ, Inc., United States of America (USA)
20.000000
20.000000
20.000000
0.69
Sanofi Pasteur, United States of America (USA)
7.000000
0.24
Sanofi US, United States of America (USA)
2.000000
0.07