Base editing rescues seizures and sudden death in a SCN8A mutation-associated developmental epileptic encephalopathy model

Journal:
Journal of Clinical Investigation
Published:
DOI:
10.1172/jci196402
Affiliations:
5
Authors:
12
Institutions Authors Share
UVA Health System, United States of America (USA)
6.500000
0.54
University of Virginia (UVA), United States of America (USA)
4.500000
0.38
University of Michigan (U-M), United States of America (USA)
1.000000
0.08