AAV-mediated gene therapy in a SLC13A5 citrate transporter disorder model rescues epileptic and metabolic phenotypes
- Journal:
- Journal of Clinical Investigation
- Published:
- DOI:
- 10.1172/jci197503
- Affiliations:
- 4
- Authors:
- 9
| Institutions | Authors | Share |
|---|---|---|
| The University of Texas Southwestern Medical Center (UT Southwestern Medical Center), United States of America (USA) | 1.00 |